It is the most common mucocutaneous inherited bleeding disorder described first by Erik Von willebrand (Finnish professor in 1926).
It has autosomal dominant inheritance found in approximately 1% of population.
It results due to germline mutations which cause either structural or quantitative abnormalities of von Willebrand Factor (vWF) leading to decreased adhesion by platelets to injured vessel wall causing impaired primary hemostasis.
Clinical Features:
Mostly patient presents with mucocutaneous bleed
Common presentations are
Epistaxis (Nasal bleed)
Menorrhagia (Heavy, prolonged menstrual periods)
Gastro intestinal bleeding
Easy bruising
Bleeding after surgery (especially involving mucus membranes)
Prolonged or excessive bleeding after dental procedures
Prolonged bleeding after delivery of a baby
May vary in each person from time to time, throughout life depending on type of von Willebrand disease
Laboratory diagnosis:
CBC to rule out thrombocytopenia as a cause of mucocutaneous bleeding.
PT and APTT to assess coagulation system.
Standard vWD test panel includes 3 stages.
Quantitative VWF test by employing enzyme immunoassay or automated latex immune assay methodology.
vWF activity test which determines the factors ability to bind to platelets. vWF function is assessed by Ristocetin agglutination test
This assay is performed by mixing the patients plasma with formalin fixed platelets and Ristocetin, a small molecule that binds and activate VWF.
Ristocetin induces multivalent VWF multimers to bind platelet glycoprotein –Ib-1X and form interplatelet” bridges”
The resulting clumping (agglutination) of platelets is measured in a device called an aggregometer.
Degree to which patient plasma promotes ristocetin dependent platelet aggulatination reflects the vWF activity of the sample.
vWF multimer analysis by sodium doclecy sulphate polyacrylamide gel electophoresis to further differentiate between vWD subtypes 2A & 2B.
References
Elaine M. Keohane, Larry J Smith, Jeanine M. Walenga. Rodaks Haematology: Clinical Principles and Applications. Fifth edition
Vinay kumar, Abul K.Abbas, Jon C. Aster. Robbins and Cotran. Pathologic Basis of Disease. 9th edition
Shirish M.Kawthalkar. Essentials of Haematology. Second edition